The survival graphs below illustrate outcomes of unrelated donor hematopoietic cell transplants (bone marrow, PBSC, or cord blood transplants — BMT) facilitated by the National Marrow Donor Program® (NMDP) for patients with inherited immune deficiencies and metabolic disorders.
Figure 1 shows survival curves for selected immune deficiencies.
Figure 1.
Immune deficiencies: Survival of pediatric marrow transplant patients 2000-2009. (NMDP data)
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Figure 2 shows survival curves for inherited metabolic disorders: Hurler syndrome (also known as mucopolysaccharidosis type I, or MPS-I), and adrenoleukodystrophy/metachromatic leukodystrophy (ALD/MLD).
Figure 2.
Inherited metabolic disorders: Survival of pediatric marrow transplant patients 2000-2009. (NMDP data)
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